#Genomics / Postgenomics #Biotherapies #Synthetic biology #Systems Biology
- Gene therapy
- Rare diseases, Immunodeficiency, Wiskott-Aldrich syndrome, Chronic granulomatous disease, Fanconi anemia, Muscular dystrophies, Myotubular myopathy, Limb-girdle muscular dystrophy, Crigler-Najjar syndrome
- Clinical trials
- Hematopoietic stem cells
- Liver
- Lentiviral vectors, Adeno-associated virus vectors
- CRISPR-Cas9
- Imaging cytometry
Supervisions :